Awards & Recognition
★2021 California Life Sciences Pantheon Leadership Award
★2019 BIO Henri A. Termeer Biotechnology Visionary Award
★Lifetime Achievement Award from National MPS Society
★Roscoe O. Brady Award for Innovation and Accomplishment from WORLDSymposium
★Life Science Leadership Award from California Life Sciences
Notable Facts
→CEO and Founder of publicly-traded Ultragenyx Pharmaceutical (NASDAQ: RARE) since 2010
→Pioneered enzyme replacement therapy for MPS I at Harbor-UCLA
→Co-authored 'Saving Ryan' book published in 2022 about rare disease drug development
→Founded EveryLife Foundation for Rare Diseases in 2009
→Led development of multiple FDA-approved rare disease therapies at BioMarin
→MD/PhD from UCLA, board certified in pediatrics and medical genetics
→Has Wikipedia page documenting his career achievements